What are the key drivers and resistors for development of diagnostics and therapeutics in orphan diseases?

How to build a value proposition and sustainable business plan in this setting?

When moving outside R&D, which additional challenges arise?

How to design clinical trials and establish strategic partnerships?

Which efforts can be undertaken to ensure access and affordability of orphan disease drugs?

Join us to get the latest updates on breaking innovations in orphan diseases

The PROFILE project is funded by the H2020 programme of the European Union.

Hoping to welcome you all in Leuven.